Pharma major Roche may have earned over a hundred times what risdiplam, a drug used to treat spinal muscular atrophy (SMA), ...

Researchers studied 118 SMA type 2 patients and saw their RULM scores stayed higher than expected had their disease kept its ...

In this episode, Hannah and I tell the origin story of my disability, and how doctors eventually diagnosed me with Spinal ...

He hopes to have a lasting impact on others and plans to continue to raise awareness, promote inclusion, and embrace diversity in his community.

Biotech stock Scholar Rock (NASDAQ: SRRK) was popular among investors on Wednesday after a positive new analyst note on the ...

On February 18, the top court protected Allahbadia from arrest in multiple FIRs filed over his comments during a YouTube show ...

I knew that I really needed to reach out to my community, but mainly reach out to the younger generation,” Zelaya says. “I ...

Motor improvements in SMA adults treated with Spinraza paralleled a boost in electrical impulses along nerves that supply ...