Spinal muscular atrophy (SMA) is a rare hereditary neuromuscular disorder in which the spinal cord does not form normally.

In July 2025, Novartis Pharmaceuticals conducted a Phase III multi-center, single dose (1.2 x 1014 vector genomes), ...

More Hong Kong patients suffering from spinal muscular atrophy (SMA) will be able to enjoy a government subsidy to control ...

As treatment for spinal muscular atrophy (SMA) has drastically improved over the last decade, so too have survival rates and the number of people with SMA living well into adulthood. | A new education ...

The court said Switzerland’s refusal to pay for Spinraza for a quadriplegic patient with spinal muscular atrophy did not ...

For people like 16-year-old Vivienne Liedtke, who was born with the physical disability spinal muscular atrophy, finding a ...

Remini shared an emotional tribute to the 21-year-old she met while filming the "King of Queens" sitcom: "I want people to ...

A former Winchester University student is raising funds to help with his dream of competing in the Paralympics. Ben Morris, 24, from Swindon, is raising the funds needed to train in the sport of ...

Panelists discuss how exciting ongoing research efforts are expanding similar gene therapy technologies to other muscular ...

After a season of regulatory upheaval, obesity and rare genetic diseases will likely remain major themes for biopharma in ...

Biogen Inc. (NASDAQ:BIIB) is one of the 13 Cheap Healthcare Stocks with Huge Upside Potential. In a report released on July 7 ...

Youngster with rare muscle condition requires round-the-clock care from taxi-driving mum who turns cab into a haven of love ...