These types of mistakes are often described as “never events,” a term first coined in 2002 to refer to preventable medical ...

Pharma major Roche may have earned over a hundred times what risdiplam, a drug used to treat spinal muscular atrophy (SMA), ...

Researchers studied 118 SMA type 2 patients and saw their RULM scores stayed higher than expected had their disease kept its ...

In this episode, Hannah and I tell the origin story of my disability, and how doctors eventually diagnosed me with Spinal ...

He hopes to have a lasting impact on others and plans to continue to raise awareness, promote inclusion, and embrace diversity in his community.

Biotech stock Scholar Rock (NASDAQ: SRRK) was popular among investors on Wednesday after a positive new analyst note on the ...

I knew that I really needed to reach out to my community, but mainly reach out to the younger generation,” Zelaya says. “I ...

The matter was brought to the court’s attention through an intervention plea filed by Cure SMA Foundation of India, where the ...

Motor improvements in SMA adults treated with Spinraza paralleled a boost in electrical impulses along nerves that supply ...